Search Result "aav clades"


New Recombinant Serotypes of AAV Vectors

Journal: Current Gene Therapy
Volume: 5 Issue: 3 Year: 2005 Page: 285-297
Author(s): Guangping Gao, Luk H. Vandenberghe, James M. Wilson

AAV Hybrid Serotypes: Improved Vectors for Gene Delivery

Journal: Current Gene Therapy
Volume: 5 Issue: 3 Year: 2005 Page: 299-310
Author(s): Vivian W. Choi, Douglas M. McCarty, R. Jude Samulski

Review Article

Machine-learning-guided Directed Evolution for AAV Capsid Engineering

Journal: Current Pharmaceutical Design
Volume: 30 Issue: 11 Year: 2024 Page: 811-824
Author(s):

AAV-Mediated Gene Transfer for Treatment of Hemophilia

Journal: Current Gene Therapy
Volume: 5 Issue: 3 Year: 2005 Page: 349-360
Author(s): Lixin Wang, Roland W. Herzog

AAVs Anatomy: Roadmap for Optimizing Vectors for Translational Success

Journal: Current Gene Therapy
Volume: 10 Issue: 5 Year: 2010 Page: 319-340
Author(s): Angela M. Mitchell, Sarah C. Nicolson, Jayme K. Warischalk, R. Jude Samulski

Developing Immunologically Inert Adeno-Associated Virus (AAV) Vectors for Gene Therapy: Possibilities and Limitations

Journal: Current Pharmaceutical Biotechnology
Volume: 14 Issue: 12 Year: 2013 Page: 1072-1082
Author(s): Ruchita S. Selot,Sangeetha Hareendran,Giridhara R. Jayandharan

Adeno-Associated Virus (AAV) Mediated Dystrophin Gene Transfer Studies and Exon Skipping Strategies for Duchenne Muscular Dystrophy (DMD)

Journal: Current Gene Therapy
Volume: 15 Issue: 4 Year: 2015 Page: 395-415
Author(s): Klaudia Kawecka,Michael Theodoulides,Yalin Hasoglu,Susan Jarmin,Hanna Kymalainen,Anita Le-Heron,Linda Popplewell,Alberto Malerba,George Dickson,Takis Athanasopoulos

Adeno-Associated Virus-Mediated Gene Transfer in Hematopoietic Stem/Progenitor Cells as a Therapeutic Tool

Journal: Current Gene Therapy
Volume: 6 Issue: 6 Year: 2006 Page: 683-698
Author(s): Li Zhong, Weihong Zhao, Jianqing Wu, Njeri Maina, Zongchao Han, Arun Srivastava

Adeno-associated Viral Vectors for Correction of Inborn Errors of Metabolism: Progressing Towards Clinical Application

Journal: Current Pharmaceutical Design
Volume: 17 Issue: 2 Year: 2011 Page: 2500-2515
Author(s): Frank Jacobs, Lili Wang

Production, Purification and Characterization of Adeno-Associated Vectors

Journal: Current Gene Therapy
Volume: 10 Issue: 6 Year: 2010 Page: 423-436
Author(s): Eduard Ayuso, Federico Mingozzi, Fatima Bosch

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